Gene therapy

Researchers from Amsterdam University Medical Center (Amsterdam UMC), in collaboration with leading clinical centers across 11 countries, have successfully completed the world’s first Phase...

Cardiovascular disease remains the leading cause of mortality worldwide. Despite decades of monumental progress in prevention and treatment, it continues to claim millions of...

The U.S. Food and Drug Administration (FDA) has officially approved the first gene therapy for the treatment of a rare form of hereditary hearing...

According to a new study published in the journal Nature, an experimental gene therapy has demonstrated high efficacy and safety in restoring hearing for...

In the modern world, one of the primary drivers of obesity is the easy accessibility of high-calorie, palatable food. People often consume food not...

Spinal Muscular Atrophy (SMA) is a rare neuromuscular disease that causes progressive muscle weakness and affects the ability to breathe, swallow, and move. It...

For the first time in history, researchers have been able to slow the progression of Huntington's disease, a condition previously considered incurable. The gene...

Diseases caused by toxic proteins, such as Creutzfeldt-Jakob syndrome (CJD), may soon become curable. A molecular editor called CHARM effectively "turns off" the disease...